A single gene therapy injection has shown the ability to restore hearing in patients with a specific genetic mutation, with ...

Children with hereditary deafness regained their hearing thanks to a type of gene therapy, a new study published on Wednesday found. In a clinical trial, co-led by investigators from Mass Eye and Ear, ...

A groundbreaking gene therapy trial has successfully restored hearing in individuals with a rare form of congenital deafness.

RMAT designation enables intensified FDA engagement and potential accelerated pathways, implying preliminary clinical evidence for RTx-015 despite absent peer-reviewed efficacy details, endpoints, and ...

USA: In an interim analysis of the phase I/II BEACON study, treatment with ristoglogene autogetemcel (risto-cel) demonstrated ...

The first study to evaluate both eyes treated with a gene therapy targeting neovascular, or wet, age-related macular degeneration (AMD) has found the treatment as safe and effective in the second eye ...

Results from the largest cohort of children who received a gene therapy for a rare immunodeficiency condition have shown the long-term safety and efficacy of the curative treatment, in a study led by ...

Researchers say deafness can affect children's brain development. Children with hereditary deafness regained their hearing thanks to a type of gene therapy, a new study published on Wednesday found.