Merck (known as MSD outside the US) has announced an agreement with the US government to provide key products to patients at ...

Novo Nordisk’s Wegovy (semaglutide) pill has been approved by the US FDA as an oral weight loss medication. In addition to ...

Every year, we’re met with restructuring, hiring freezes, and portfolio cuts. And every year we tell ourselves the same story ...

Montez, Medscape’s Rare Disease Education Lead recently spoke with Dr Lucy McKay, CEO, and Megan Pullein, Strategic Operations Officer from the UK-based charity Medics for Rare Disease (MfRD). We ...

How was a new rare disease discovered through Singapore’s Undiagnosed Disease Program? And how will technology allow us to ...

Discover how AI-powered tools are transforming rare disease diagnosis, patient care, and clinical decision-making.

For a child with a rare disease, a doctor’s continuing education can end a years-long diagnostic odyssey and unlock access to ...

Nurses play a vital and multifaceted role in rare disease care, providing consistent patient support, education, and care ...

CGT Catapult, an independent technology organisation specialising in the cell and gene therapy (CGT) industry, has established ReCell, a consortium focusing on safety tests for a range of cell ...

The US FDA has announced the launch of the Technology-Enabled Meaningful Patient Outcomes (TEMPO) for Digital Health Devices Pilot, designed to promote safe access to digital health devices. The pilot ...

Pfizer has announced results from its phase 3 BASIS study of Hympavzi (marstacimab), demonstrating its success in reducing bleeds in adults and adolescents living with haemophilia A or B with ...

Vandria has announced positive topline results from the first-in-human clinical trial of its lead candidate VNA-318, supporting its possible application in treating Alzheimer’s disease (AD). VNA-318, ...